Search for Clinical Trial Results
Hurler Syndrome - 26 Studies Found
Status | Study |
Recruiting |
Study Name: BMT Abatacept for Non-Malignant Diseases Condition:
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Recruiting |
Study Name: MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis Condition:
Interventions: |
Active, not recruiting |
Study Name: Allogeneic Bone Marrow Transplant for Inherited Metabolic Disorders Condition:
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Recruiting |
Study Name: Mucopolysaccharidosis I (MPS I) Registry Condition: Mucopolysaccharidosis I (MPS I) Date: 2005-09-02 |
RECRUITING |
Study Name: A Study to Investigate the Efficacy and Safety of OTL-203 in Subjects With MPS-IH Compared With Standard of Care With Allogeneic HSCT Condition: MPS-IH (Hurler Syndrome) Date: 2024-05-19 Interventions: Experimental: OTL-203: Autologous CD34+ enriched cell fraction that contains hematopoietic stem and progenitor cells transduced ex vivo using lentivir |